BETA TALASEMIJA MAJOR (PEDIJATRIJA)
Farmakološka indukcija sinteze fetalnog hemoglobina
srpski (latinica)
Farmakološka indukcija sinteze fetalnog hemoglobina
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Beta talasemija major (pedijatrija)

Farmakološka indukcija sinteze fetalnog hemoglobina

Terapija (hidroksikarabamidom) hidroksiureom

Efficacy of hydroxyurea in providing transfusion independence in β-thalassemia. (otvara novi prozor)

Ansari SH, Shamsi TS, Ashraf M, Perveen K, Farzana T, Bohray M, Erum S, Mehboob T.

Izvor‎: J Pediatr Hematol Oncol 2011;33(5):339-43.

Indeks‎: PubMed 21602718

DOI‎: 10.1097/MPH.0b013e31821b0770

https://www.ncbi.nlm.nih.gov/pubmed/21602718 (otvara novi prozor)

Gγ-Xmn I polymorphism: a significant determinant of β-thalassemia treatment without blood transfusion. (otvara novi prozor)

Ansari SH, Shamsi TS, Munzir S, Khan MT, Erum S, Perveen K, Farzana T, Ashraf M, Mehboob T, Moinuddin M.

Izvor‎: J Pediatr Hematol Oncol 2013;35(4):e153-6.

Indeks‎: PubMed 23389500

DOI‎: 10.1097/MPH.0b013e31827e8662

https://www.ncbi.nlm.nih.gov/pubmed/23389500 (otvara novi prozor)

Efficacy of hydroxyurea (HU) in reduction of pack red cell (PRC) transfusion requirement among children having beta-thalassemia major: Karachi HU trial (KHUT). (otvara novi prozor)

Ansari SH, Shamsi TS, Siddiqui FJ, Irfan M, Perveen K, Farzana T, Panjwani VK, Yousuf A, Mehboob T.

Izvor‎: J Pediatr Hematol Oncol 2007;29(11):743-6.

Indeks‎: PubMed 17984691

DOI‎: 10.1097/MPH.0b013e318157fd75

https://www.ncbi.nlm.nih.gov/pubmed/17984691 (otvara novi prozor)

Hydroxyurea can eliminate transfusion requirements in children with severe beta-thalassemia. (otvara novi prozor)

Bradai M, Abad MT, Pissard S, Lamraoui F, Skopinski L, de Montalembert M.

Izvor‎: Blood 2003;102(4):1529-30.

Indeks‎: PubMed 12702505

DOI‎: 10.1182/blood-2003-01-0117

https://www.ncbi.nlm.nih.gov/pubmed/12702505 (otvara novi prozor)

Decreased transfusion needs associated with hydroxyurea therapy in Algerian patients with thalassemia major or intermedia. (otvara novi prozor)

Bradai M, Pissard S, Abad MT, Dechartres A, Ribeil JA, Landais P, de Montalembert M.

Izvor‎: Transfusion 2007;47(10):1830-6.

Indeks‎: PubMed 17880608

DOI‎: 10.1111/j.1537-2995.2007.01399.x

https://www.ncbi.nlm.nih.gov/pubmed/17880608 (otvara novi prozor)

Genotype-phenotype relationship of patients with β-thalassemia taking hydroxyurea: a 13-year experience in Iran. (otvara novi prozor)

Karimi M, Haghpanah S, Farhadi A, Yavarian M.

Izvor‎: Int J Hematol 2012;95(1):51-6.

Indeks‎: PubMed 22180324

DOI‎: 10.1007/s12185-011-0985-6

https://www.ncbi.nlm.nih.gov/pubmed/22180324 (otvara novi prozor)

A randomised double-blind placebo-controlled clinical trial of oral hydroxyurea for transfusion-dependent β-thalassaemia. (otvara novi prozor)

Yasara N, Wickramarathne N, Mettananda C, Silva I, Hameed N, Attanayaka K, Rodrigo R, Wickramasinghe N, Perera L, Manamperi A, Premawardhena A, Mettananda S

Izvor‎: Sci Rep. 2022;12(1):2752.

Indeks‎: PubMed 35177777

DOI‎: 10.1038/s41598-022-06774-8

https://pubmed.ncbi.nlm.nih.gov/35177777/ (otvara novi prozor)

Response to hydroxyurea treatment in Iranian transfusion-dependent beta-thalassemia patients. (otvara novi prozor)

Yavarian M, Karimi M, Bakker E, Harteveld CL, Giordano PC.

Izvor‎: Haematologica 2004;89(10):1172-8.

Indeks‎: PubMed 15477200

https://www.ncbi.nlm.nih.gov/pubmed/15477200 (otvara novi prozor)

Hydroxyurea therapy in 49 patients with major beta-thalassemia. (otvara novi prozor)

Zamani F, Shakeri R, Eslami SM, Razavi SM, Basi A.

Izvor‎: Arch Iran Med 2009;12(3):295-7.

Indeks‎: PubMed 19400608

https://www.ncbi.nlm.nih.gov/pubmed/19400608 (otvara novi prozor)

Rekombinovani eritropoetin (sam ili u kombinaciji sa drugim lekovima)

Use of hydroxyurea and recombinant erythropoietin in management of homozygous ß⁰ thalassemia. (otvara novi prozor)

Kohli-Kumar M, Marandi H, Keller MA, Guertin K, Hvizdala E.

Izvor‎: J Pediatr Hematol Oncol 2002;24(9):777-8.

Indeks‎: PubMed 12468925

https://www.ncbi.nlm.nih.gov/pubmed/12468925 (otvara novi prozor)

Drugi lekovi

Fetal globin gene inducers: novel agents and new potential. (otvara novi prozor)

Perrine SP, Castaneda SA, Chui DH, Faller DV, Berenson RJ, Siritanaratku N, Fucharoen S.

Izvor‎: Ann N Y Acad Sci 2010;1202:158-64.

Indeks‎: PubMed 20712788

DOI‎: 10.1111/j.1749-6632.2010.05593.x

https://www.ncbi.nlm.nih.gov/pubmed/20712788 (otvara novi prozor)